Accelerating Cell & Gene Therapy Adoption:
Proof of Concept to Standard of Care

Plenary and Satellite Sessions
Translational Research
Clinical Translation
Commercialization
Hot Topics Sessions
Strategies for Commercialization Track
Quality and Operations Track

TUESDAY MAY 26

07:00 – 17:00
FACT Cord Blood Inspection and Accreditation Workshop

16:00 – 19:00
ISCT 2020 Registration Open

WEDNESDAY MAY 27 - Pre-Conference Day

PRECONFERENCE TRACKS

MSC​

CO-CHAIRS
Jacques Galipeau, MD
University of Wisconsin-Madison (US)

Mauro Krampera, MD
University of Verona (IT)

Luc Sensebe, MD, PhD
ISCT MSC Committee (FR)

08:30 – 10:00
MSC in Normal and Pathological Tissue Microenvironment

10:15 – 11:45
MSC-derived Extracellular Vesicles: Certainty and Perspectives

13:00 – 14:30
MSC Manufacturing for Clinical Use and Regulatory Issues

14:45 – 16:15
MSC-based Clinical Trials Worldwide

Cell Processing

CO-CHAIRS
Ruud Hulspas, PhD
Cellular Technologies Bioconsulting, LLC (NL)

Mara Neal, SH(ASCP)MT, MS, MBA
Cook Biotech (US)

Vicki Antonenas, MSc
Westmead Hospital
(AU)

Paul Wallace, PhD
Roswell Park Comprehensive Cancer Center (US)

08:30 – 10:00
Collection and Starting 
Materials

10:15 – 11:45
Selection of cells
and gene editing

13:00 – 14:30
Cell Activation and
Expansion

14:45 – 16:15
Product Characterization, just before product goes to patient

Global Regulatory Perspectives

CO-CHAIRS
Karen Nichols, Esq.
Magenta Therapeutics (US)

Dominic Wall, PhD, FFSc (RCPA)
Cell Therapies Pty Ltd, Peter MacCallum Cancer Centre (AU)

08:00 – 08:30
Regulatory Roundup

08:30 – 10:00
Sterility Controls –
Past, Present, Future

10:15 – 11:45
Post Processing
Manufacturing

13:00 – 14:30
Combination Products (Biologics/Devices)

14:45 – 16:15
Topic TBC

Investigators to Investors
(i to i)

CO-CHAIRS
Bill Milligan
Steminent Biotherapeutics (CA/TW)

Patrick Rivers
Aquilo Capital (US)

Program under development

ISCT-Cord Blood Connect
In partnership with WMDA

CO-CHAIRS
Elizabeth J. Shpall, MD
MD Anderson Cancer Center (US)

Joanne Kurtzberg, MD
Carolina’s Cord Blood Bank Duke University Medical Center (US)

Ngaire Elwood, PhD
BMDI Cord Blood Bank and Murdoch Children’s Research Institute (AU)

Program under development

Corporate Symposia

16:30 – 18:30

Technology Symposium

MB_Logo

 16:30 – 18:30

Technology Symposium

Thermo-Fisher-COLOR-CMYK

19:00 – 19:30

President’s Welcome Address

J. Rasko_cropped

John Rasko, AO, BSc(Med), MBBS(Hons), PhD
University of Sydney (AU)

ISCT President

capecchi_cropped

Mario Capecchi, PhD
University of Utah (US)

2007 Nobel Laureate
(Physiology or Medicine)

C. Chabbanon_cropped

Christian Chabannon, MD, PhD
Institut Paoli Calmettes (FR)
ISCT 2020 Co-Chair

R. Ciccocioppo_cropped

Rachele Ciccocioppo, MD
University of Verona 
(IT)
ISCT 2020 Co-Chair

I. Martin_cropped

Ivan Martin, PhD
University Hospital Basel 
(CH)
ISCT 2020 Co-Chair

19:30 – 21:00

Exhibit Open House and Welcome Reception

Open to all registered delegates, enjoy a glass of wine, hors d’oeuvres, and the opportunity to mingle and network
with peers from all over the globe. 
Make new connections and discover the latest innovations and services from our exhibitors.  

Global Showcase Theatre (Exhibit Hall)

20:00 – 20:15
Sexton Biotechnologies

20:15 – 20:30 
Open

THURSDAY MAY 28 - Day One Main Meeting

07:30 - 08:30
Hot Topics Session

Regenerative Medicine in Digestive Diseases: State of the Art, Open Needs and Next Steps

C0-CHAIRS
Basak E. Uygun, PhD,
Massachusetts General Hospital and Harvard Medical School (US)
Giuseppe Orlando, PhD,
Wake Forest Institute and School of Medicine (US)

SPEAKERS
Khalil N. Bitar, PhD,
Wake Forest School of Medicine (US)
Vincenzo Cardinale, MD, PhD,
Sapienza University of Rome (IT)
Pedro Baptista, PharmD, PhD,
Madrid University and Aragon Institute for Health Research (ES)

07:30 - 08:30
Hot Topics Session

Gene Edited and Engineered Cell Based
Therapeutics for Cancer

CO-CHAIRS
Khalid Shah, MS, PhD,
Harvard Medical School (US)
Massimo Dominici, MD,
University of Modena and Reggio Emilia (IT)

07:30 - 08:30
Corporate Session

Breakfast Tutorial Hosted by

08:30 – 10:30

Opening Remarks
ISCT Career Achievement Award Presentation

 

Presidential Plenary
Mastering Pluripotent Cells with Therapeutic Intent

CHAIR

J. Rasko_cropped

John Rasko, AO, BSc(Med), MBBS(Hons), PhD
University of Sydney (AU)

translational research_cropped
capecchi_cropped

Mario Capecchi, PhD 
University of Utah (US)

2007 Nobel Laureate (Physiology or Medicine)
Keynote speaker sponsored by Cytotherapy, The official journal of the International Society for Cell & Gene Therapy

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M. Pechanski_cropped

Marc Peschanski, MD, PhD 
I-Stem (FR)

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R. Jaenisch_cropped

Rudolf Jaenisch, MD   
Whitehead Institute and Massachusetts Institute of Technology (US)

Break

10:30 – 11:00
Coffee Break with Exhibits and Corporate Sessions

Global Showcase Theatre (Exhibit Hall)

10:30 – 10:45 
GenScript

10:45 – 11:00 
Sartorius

11:00 - 12:15
Plenary Satellite 1a

iPSC for Cardiovascular Disease

11:00 - 12:15
Plenary Satellite 2a

MSC Mechanism of Action

CHAIR
Jacques Galipeau, MD,
University of Wisconsin-Madison (US)

SPEAKER
Karin Tarte, PharmD, PhD,
University of Rennes (FR)

11:00 - 12:15
Workshop

Gene Therapy for Globin Disorders

11:00 - 12:15
Strategies for Commercialization

Innovating Process Development for Sustainable Manufacturing

CHAIR
Dominic Clarke, PhD,
HemaCare Corp. (US)

SPEAKERS
Denis Bedoret, PhD,
Masthercell (BE)
Stuart Curbishly, PhD, 
Birmingham University NHS Trust (UK)
Ricardo Batista, PhD, 
Cellectis (FR)

11:00 - 12:15
Quality & Operations

Qualification, Regulation of Gene Editing Tools in Cell & Gene Therapy

CHAIR
Shirley Bartido, PhD, 
Cellectis (US)

SPEAKERS
Christopher Ballas, PhD, 
Rocket Pharma (US)
David R. JonesFRSB, FBTS, 
MHRA (UK)
Stephan Reynier, MSc, 
Cellectis (FR)

Break

12:15 – 13:45
Lunch with Exhibits and Corporate Sessions

Lunch & Learn Session
(Lunch Provided)

12:30 – 13:30


Lunch & Learn Session
(Lunch Provided)

12:30 – 13:30

 

Global Showcase Theatre (Exhibit Hall)

12:30 – 12:45

12:45 – 13:00  Cynata

13:00 – 13:15 

13:15 – 13:30 

13:45 – 15:15

Plenary
Mesenchymal Stromal Cells – Full Circle from Basic Research Insights to Clinical Trial Updates

CHAIR

S. Viswanathan_cropped

Sowmya Viswanathan PhD
University Health Network Cell Therapy (CA)

translational research_cropped
J. Galipeau_cropped

Jacques Galipeau, MD
University of Wisconsin-Madison (US)

clinical translation_cropped
H. Bonig_cropped

Halvard Bönig, MD, PhD
Johann-Wolfgang-Goethe University  (DE)

clinical translation_cropped
D. Farge Bancel_cropped

Dominique Farge Bancel, MD
Paris Diderot University and Hopital Saint-Louis (FR)

Break

15:15 – 15:45
Coffee Break with Exhibits and Corporate Sessions

Global Showcase Theatre (Exhibit Hall)

15:15 – 15:30 
New Jersey Innovation Institute

15:30 – 15:45 
TreeFrog Therapeutics

15:45 - 17:00
Plenary Satellite 1b

iPSC Derived Organoids

 

15:45 - 17:00
Plenary Satellite 2b

Opportunities, Challenges and Tangible Progress in the Development of Efficacious Culture Expanded Cell Therapies for Musculoskeletal Disease

MODERATOR
George Muschler, MD,
Cleveland Clinic (US)

SPEAKERS
Christian Jorgensen, MD, PhD,
University Hospital Lapeyronie (FR)
Scott Rodeo, MD,
The Hospital for Special Surgery (US)
Nicolas Piuzzi, MD,
Cleveland Clinic (US)

15:45 - 17:00
Workshop

Success and Failure of Cell Therapy Clinical Trials for Acute and Chronic Lung Disease

CO-CHAIRS
Patricia R. M. Rocco, MD, PhD,
Federal University of Rio de Janeiro (BR)
Claudia Dos Santos, MD,
University of Toronto (CA)

15:45 - 17:00
Strategies for Commercialization

Can we industrialize CAR T therapies? The practical challenges in achieving wide-spread patient access

CHAIR
Bill Milligan,
Steminent Biotherapies (US/TW)

SPEAKERS
Gunther Busam, RPh, PhD, 
Celgene (CH)

Elizabeth Hexner, MD,
Penn Medicine (US)
Wen Bo Wang, PhD,
Fate Therapeutics (US)

15:45 - 17:00
Quality & Operations

Manufacturing Process Validation – Considerations for Validation of Autologous Products

CHAIR
Emily Hopewell, PhD,
Indiana University School of Medicine (US)

SPEAKERS
Antonio Ruiz-Garcia, MPharm,
Hospital Universitario Virgen de las Nieves (SP)
Aisha Khan, MSc, MBA,
University of Miami (US)

Corporate Sessions

17:00 – 19:00
Therapeutic Symposium

17:30 – 18:30
Technology Spotlight

Posters & Abstract Presentations

Poster Hall

18:00 – 19:30
Poster Session

Global Showcase Theatre (Exhibit Hall)

18:00 – 18:30
Abstract Elevator Pitch Session 1

FRIDAY MAY 29 - Day Two Main Meeting

Hot Topics

07:30 – 08:30
Long-Term Follow-up, Accreditation and Registries for
CAR-T Therapy (Joint Session with EBMT)

07:30 – 08:30
Veterinary Medicine

08:45 – 10:15

Plenary
Advances and Emerging Technologies in Immune-Mediated Cancer Treatments

CO-CHAIR

B. Levine_cropped

Bruce Levine, PhD
University of Pennsylvania (US)

CO-CHAIR

C. Chabbanon_cropped

Christian Chabannon, MD, PhD
Institut Paoli Calmettes (FR)

translational research_cropped
M. Maus_cropped

Marcela Maus, MD, PhD
Massachusetts General Hospital and Harvard Medical School (US)

translational research_cropped
M. Hudacek_cropped

Michael Hudecek, MD
University of Würzburg (DE)

clinical translation_cropped
K. Rezvani_cropped

Katy Rezvani, MD, PhD
MD Anderson Cancer Center (US)

Break

10:15 – 10:45
Coffee Break with Exhibits and Corporate Sessions

Global Showcase Theatre (Exhibit Hall)

10:15 – 10:30
VivaBioCell

10:30 – 10:45 
RoosterBio

10:45 - 12:15
Plenary Satellite 3a

Immunotherapy Oral Abstracts

 

10:45 - 12:15
Plenary Satellite 4a

Industrializing Clinical Delivery

CHAIR
Simon Ellison, MBA,
World Courier (UK)

SPEAKERS
Jacqueline Barry, PhD,
Cell and Gene Therapy Catapult (UK)

10:45 - 12:15
Workshop

Imaging Cellular Therapeutics
(Joint Session with HESI CT-TRACS)

10:45 - 12:15
Workshop

ISCT Presidential Task Force Session

10:45 - 12:15
Strategies for Commercialization

Raising Capital for CGT Industralization

CHAIR
Patrick Rivers, MBA,
Aquilo Capital (US)

SPEAKER
Jak Knowles, MD, 
Century Therapeutics (US)

10:45 - 12:15
Quality & Operations

Regulatory CMC Considerations Across CGT

CHAIR
Paula Salmikangas, PhD
NDA Advisory Services Ltd. (FI)

SPEAKERS
Christopher Bravery, PhD, 
Consulting on Advanced Biologicals Ltd (UK)
Shinichi Noda, PhD
Pharmaceuticals and Medical Devices Agency (PMDA) (JP)
Rocio Salvador-Roldan,
European Commission (BE)
 

Break

12:15 – 13:45
Lunch with Exhibits and Corporate Sessions

Lunch & Learn Session
(Lunch Provided)

12:30 – 13:30

 

Lunch & Learn Session
(Lunch Provided)

12:30 – 13:30

Global Showcase Theatre (Exhibit Hall)

12:30 – 12:45 
12:45 – 13:00 

13:00 – 13:15  Xcell Therapeutics

13:15 – 13:30  Be the Match

13:45 – 15:15

Plenary
Is Big Pharma ready for industrial scale Cell and Gene Therapy?

CHAIR

A. Ting_cropped

Anthony Ting, PhD 
Athersys (US)

commercialization_cropped
E. Ostuni_cropped

Emanuele Ostuni, PhD
Novartis Oncology (CH)

translational research_cropped
A. Krackhardt

Angela Krackhardt, MD
Technical University of Munich (DE)

commercialization_cropped
A. Santagostini_cropped

Alberto Santagostino, MBA
Lonza (CH)

Break

15:15 – 15:45
Coffee Break with Exhibits and Corporate Sessions

Global Showcase Theatre (Exhibit Hall)

15:15 – 15:30
Cell-Easy

15:30 – 15:45 
Open

15:45 - 17:00
Plenary Satellite 3b

CAR-T for Solid Tumors

 

15:45 - 17:00
Plenary Satellite 4b

Industrializing administration setting

CHAIR
Julie Murrell

SPEAKERS
Christopher Herbert, PhD,
Leeds Teaching Hospitals NHS Trust (UK)
Anne Black,
NHS Specialist Pharmacy Service (UK)
Christoph Demmerle,
Novartis (DE)

15:45 - 17:00
Workshop

ISCT Chief Scientific Officer Abstract Showcase

15:45 - 17:00
Workshop

Early Stage Professionals Session

15:45 - 17:00
Strategies for Commercialization

Best practices for funding CGT startups from academia

CHAIR
Patrick Rivers, MBA, 
A
quilo Capital (US)

SPEAKERS
Mike Milone, MD, PhD, 
Cabaletta Bio (US)
Colleen Delaney, MD, MSc, 
Nohla Therapeutics (US)

15:45 - 17:00
Quality & Operations

Starting & Raw Material Selection for ATMP Manufacturing

CHAIR
Gloria Carmona, MPharm
Andalusian Network for Design and Translation of Advanced Therapies (ES)

SPEAKERS
Craig Spalding, MBA
Scottish National Blood Transfusion Service (UK)
Rosaria Giordano, MD
University Hospital of Milano (IT)
Daniela Bischof, PhD,
 Indiana University School of Medicine (US)

Gerhard Bauer, PhD, 
University of California Davis Institute for Regenerative Cures (US) 

Posters & Abstract Presentations

Poster Hall

18:00 – 19:30
Poster Session

Global Showcase Theatre (Exhibit Hall)

18:00 – 18:30
Abstract Elevator Pitch Session 1

SATURDAY MAY 30 - Day Three Main Meeting

08:00 - 09:00
Hot Topics Session

The spleen plays a critical role in modulating therapeutic outcomes following administration of cellular therapies in acute treatment settings

 

08:00 - 09:00
Hot Topics Session

Safety Matters for Regenerated Tissues
(Joint Session with TERMIS EU)

08:00 - 09:00
Strategies for Commercialization

Providing effective cellular therapies in the face of commercialization – meeting patients’ needs and expectations

CHAIR
Gerhard Bauer, PhD
University of California, Davis Institute for
Regenerative Cures (US)

SPEAKERS
Kathryn Rodden
NHS University Hospitals of Birmingham (UK)
Mohamed Abou-El-Enein, MD, PhD
Charité – Universitätsmedizin Berlin (DE)
Mark Yarborough, PhD
University of California, Davis (US)

08:00 - 09:00
Quality & Operations

Characterization of Active Substance and Comparability

CHAIR
Rosemarie Bell, B.App.Sc Micro/Biochem MASM
Q-Gen Cell Therapeutics QIMR Berghofer Medical Research Institute (AU)

SPEAKERS
Mehrshid Alai-Safer, PhD
Kite Pharmaceuticals (US)
Mohamed Heidaran, PhD
Parexel International (US)
Krishnendu Roy, PhD
Georgia Institute of Technology (US)

09:15 – 10:45

Plenary
Gene Engineering: The Past, Present and the Future

CHAIR

S. Soni_cropped

Sandeep Soni, MD 
Stanford University (US)

translational research_cropped
D. Kohn_cropped

Donald Kohn, MD
University of California Los Angeles (US)

translational research_cropped
P. Rio_cropped

Paula Rio, PhD
Centro de Investigaciones Energéticas
Medioambientales y Tecnológicas (CIEMAT) (SP)

clinical translation_cropped
C. Fonck_cropped

Carlos Fonck, PhD
DABT, BioMarin Pharmaceuticals Inc. (US)

10:45 – 11:00
Coffee Break

11:00 - 12:00
Plenary Satellite 5a

Gene Therapy Clinical Trials

11:00 - 12:00
Plenary Satellite 6a

EV Technical Session

CHAIR
Clotilde Thèry, PhD,
Institut Curie, INSERM (FR)

SPEAKER
An Hendrix, PhD

Ghent University (BE)

11:00 - 12:00
Workshop

Late Breaking Oral Abstracts

11:00 - 12:00
Strategies for Commercialization

Clinical experience in regenerative medicine and tissue engineering, the next wave of advanced therapies

CHAIR
Julie Allickson, PhD
Wake Forest Institute for Regenerative Medicine (US)

SPEAKERS
Petter Björquist, PhD
VERIGRAFT AB (SE)
Martin Birchall, MD
University College London (UK)
Heather Prichard, PhD
Humacyte (US)

11:00 - 12:00
Quality & Operations

Analytical Tools and Method Development 

CHAIR
Gerry McKiernan, 
Cell Therapies Pty Ltd (AU)

SPEAKER
Sophie Paczensy, MD, PhD, 
Indiana University School of Medicine (US)

12:00 – 13:30
Lunch

12:15 – 13:15
ISCT Annual General Business Meeting
(All Members Invited)

13:30 – 15:00

Plenary
Basics and translational potential of extracellular vesicles including exosomes

CHAIR

B. Giebel

Bernd Giebel, PhD 
University Hospital Essen
Institute for Transfusion (DE)

translational research_cropped
C. Thery_cropped

Clotilde Théry, PhD
Institut Curie, INSERM (FR)

translational research_cropped
SK. Lim_cropped

Sai-Kiang Lim, PhD
Institute of Medical Biology, A*STAR (SG)

translational research_cropped
R. Lim_cropped

Rebecca Lim, PhD
Monash University (AU)

15:00 – 15:15
Coffee Break

15:15 - 16:30
Plenary Satellite 5b

Ex-Vivo Stem Cell Based Clinical Trials

SPEAKER
Sandeep Soni, MD,
Stanford University (US) 

 

15:15 - 16:30
Plenary Satellite 6b

ISCT-ISEV Joint Session: MSC-EVs

SPEAKER
Mario Gimona, PhD,
Paracelsus Medical University (AT)

15:15 - 16:30
Workshop

Early Stage Professionals Session

15:15 - 16:30
Strategies for Commercialization

Fast Track Regulations

CHAIR
Siofradh McMahon, MSc, 
CCRM (CA)

SPEAKER
Katy Spink, PhD, 
Dark Horse Consulting (US)

15:15 - 16:30
Quality & Operations

GMP Manufacturing Challenges 

CHAIR
Shiraz Ziya, PhD, 
Sartorius Stedim UK Ltd (UK)

SPEAKER
Angela Osborne, PhD, 
eXmoor pharma concepts ltd (UK)
Linda Kelley, PhD, 
Moffitt Cancer Center (US)